Search for Clinical Trial Results
Mucopolysaccharidosis Type IV - 47 Studies Found
Status | Study |
Recruiting |
Study Name: A Multicenter, Multinational, Observational Morquio A Registry Study (MARS) Condition:
Interventions: Drug: Vimizim® (elosulfase alfa) Recombinant human N acetylgalactosamine 6 sulfatase (rhGALNS) |
Completed |
Study Name: Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Condition:
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Recruiting |
Study Name: Longitudinal Studies of Brain Structure and Function in MPS Disorders Condition:
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Enrolling by invitation |
Study Name: Identification and Characterization of Bone-related Genetic Variants in Families Condition: Skeletal Dysplasia Date: 2015-12-16 Interventions: Other: Samples With DNA After consenting, all subjects hav |
Completed |
Study Name: A Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IVA Condition: MPS IV A Date: 2009-04-10 Interventions: Drug: BMN 110 Subjects will receive a weekly 4- to 5-hour |
Terminated |
Study Name: Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics Condition:
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Completed |
Study Name: A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Condition: MPS IV A Date: 2011-01-10 Interventions:
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Terminated |
Study Name: Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA Condition: Mucopolysaccharidosis Type IVA Date: 2012-11-21 |
Approved for marketing |
Study Name: BMN 110 US Expanded Access Program Condition:
Date: 2013-05-15 Interventions: Drug: BMN 110 |
Terminated |
Study Name: A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Condition:
Date: 2010-10-28 Interventions: Drug: BMN 110 Patients will receive an intravenous infusion of BMN110 at 2.0mg/kg/week, over a period of |